TitleAllele-Specific Gene Editing Rescues Pathology in a Human Model of Charcot-Marie-Tooth Disease
Publication TypeJournal Article
Year of Publication2021
AuthorsFeliciano, CM, Wu, K, Watry, HL, Marley, CBE, Ramadoss, GN, Ghanim, HY, Liu, AZ, Zholudeva, LV, McDevitt, TC, Saporta, MA, Conklin, BR, Judge, LM
JournalFrontiers in Cell and Developmental Biology
Date PublishedApril 2022
DOI10.3389/fcell.2021.72302310.3389/fcell.2021.723023.s00110.3389/fcell.2021.723023.s002
Short TitleFront. Cell Dev. Biol.